The first gene therapy (somatic enzyme) was successfully done in
Correct Answer: SCID
Description: Deficiency of adenosine deaminase, a condition that affects lymphocytes paicularly, was the first disease to be treated by gene therapy. Deficiency of adenosine deaminase accounts for 15% of all cases of severe combined immunodeficiency (SCID)In 1990, Dr. William French Anderson introduced a new copy the gene, carried on a retroviral vector, into a 4-year-old girl suffering from severe combined immunodeficiency (Bubble boy disease).Ref: Harper 30th edition pg: 699
Category:
Biochemistry
Get More
Subject Mock Tests
Practice with over 200,000 questions from various medical subjects and improve your knowledge.
Attempt a mock test nowMock Exam
Take an exam with 100 random questions selected from all subjects to test your knowledge.
Coming SoonGet More
Subject Mock Tests
Try practicing mock tests with over 200,000 questions from various medical subjects.
Attempt a mock test now